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Mucopolysaccharidosis Type VI - 35 Studies Found
Estado | Estudiar |
Recruiting |
Nombre del estudio: Effects of Adalimumab in Mucopolysaccharidosis Types I, II and VI Condición:
Intervenciones: |
Completed |
Nombre del estudio: Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease Condición:
Fecha: 2012-10-12 Intervenciones: Other: Enzyme testing Leukocyte activity measurement of Arylsulfatase B and N acetyl galactosamine 6 sul |
Completed |
Nombre del estudio: Stem Cell Transplantation for Hurler Condición:
Intervenciones: |
Terminated |
Nombre del estudio: Clinical Trial of Growth Hormone in MPS I, II, and VI Condición:
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Recruiting |
Nombre del estudio: Longitudinal Studies of Brain Structure and Function in MPS Disorders Condición:
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Terminated |
Nombre del estudio: Mucopolysaccharidosis (MPS) I, II, and VI Screening in a High-Risk Population With Previous Surgical Repair or Presence of Inguinal and/or Umbilical Hernia in Combination With Pediatric ENT Surgery (The HATT Project) Condición:
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Recruiting |
Nombre del estudio: Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children Condición:
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Terminated |
Nombre del estudio: Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics Condición:
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Terminated |
Nombre del estudio: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation Condición:
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